Regional Medical Science Liaison - Europe, Named Patient Programs

Location:
Remote role based in The Netherlands, France, Italy, or Germany, with the ability to travel extensively across Europe (approximately 60% travel).

Purpose of the rol:

The Regional Medical Science Liaison (MSL) is responsible for the Named patient program execution cross-functionnally in Europe excluding Germany, France, Italy and UK. The role consists in building strong scientific relationships with healthcare professionals, Key Opinion Leaders (KOLs) and rare disease experts across European markets, supporting Pharming's ambition to expand access to innovative treatments for patients living with rare diseases.

The role focuses on supporting the medical and scientific aspects of Named Patient Programs (NPP), engaging with treatment centres and physicians caring for PID, APDS diagnosed patients and patients receiving Leniolisib, and facilitating appropriate collaboration to support sustainable patient access pathways. Working with partners, access team, liaising from patients to pharmacy to ensure treatment is delivered.

Working closely with International Medical Affairs as well as the Partner and NPP team commercial and Market Access, the Regional MSL contributes to disease awareness, scientific exchange and stakeholder engagement across Europe, while maintaining key experts relationships in Spain.

This is an entrepreneurial, field-based role requiring strong scientific expertise, agility, strategic priority setting, collaboration and a proactive "can-do" mindset to build an innovative and efficient regional medical engagement model.

Areas of responsibility:

Scientific Engagement & Expert Relationships

• Build and maintain trusted scientific relationships with KOLs, healthcare professionals and specialist treatment centres across assigned European markets.
• Engage with physicians caring for patients receiving leniolisib through NPPs to understand clinical needs, treatment experience and potential access challenges.
• Engage with physicians caring for PID / APDS patients requiring more information about leniolisib treatment
• Maintain strategic scientific relationships with key APDS experts in Spain.
• Gather and communicate medical insights to inform International Medical Affairs strategy and patient access planning.
  
  

Named Patient Program Medical Support

• Provide scientific and medical support for NPP activities, ensuring appropriate information is available to treating physicians, facilitating the patient and expert journey and ensuring product is delivered to patient.
• Identify and communicate unmet medical needs and potential barriers to continuity of treatment, collaborating with relevant internal teams on appropriate access pathways.
• Facilitate scientific dialogue and support medical aspects of NPP activities in accordance with applicable regulations and company procedures.
• Collaborate with Medical Affairs, Market Access and Partner Markets to support sustainable, compliant patient access solutions.
  
  

Medical Education

• Support scientific disease awareness initiatives focused on APDS, rare disease diagnosis and appropriate referral to specialist centres.
• Organize and participate in scientific exchanges, expert meetings and medical education activities.
• Identify opportunities for cross-country scientific collaboration and knowledge sharing.

Cross-Functional Collaboration & Execution

• Act as a scientific liaison between external experts and International Medical Affairs, Market Access, Commercial and Partner Markets teams.

Your profile:

Education

• Advanced scientific degree (PhD, PharmD, MD or equivalent) in Life Sciences, Medicine, Pharmacy or a related discipline.

Experience

• 7+ years of experience in Medical Affairs, Medical Science Liaison or scientific stakeholder engagement roles within biotechnology or pharmaceuticals.
• Experience in rare diseases, immunology or inborn errors of immunity strongly preferred.
• Experience with Named Patient Programs, early access programs or access-related medical activities preferred.
• Experience working across European markets and engaging with international experts.
• Fluent English required; additional European languages are an advantage.
• Willingness and ability to travel frequently across Europe.

We are looking for someone who:

• Builds trusted scientific partnerships and new ways of working across markets.
• Demonstrates a growth mindset, proactively identifying unmet medical needs and opportunities to improve scientific engagement.
• Brings an entrepreneurial, can-do attitude, taking ownership and finding practical solutions.
• Demonstrate the ability to adapt and to prioritise effectively projects including field visits given the large geography
• Executes with speed, agility and accountability in a dynamic international environment.
• Collaborates effectively across functions while maintaining scientific independence and integrity.
• Is highly patient-focused, scientifically credible and comfortable working autonomously.
• Is willing to travel across Europe for the majority of the time (60%)

Who we are

We’re built on a simple belief: people living with rare diseases deserve more.

Pharming is a global biotechnology company taking on some of the toughest rare disease challenges. We develop and commercialize innovative therapies for rare and ultra-rare immunological and genetic diseases with significant unmet need, where our scientific and commercial expertise, long-term commitment, and real partnership can help advance care.

We put patients at the heart of our work. Their insights, along with those of caregivers, clinicians, scientists, and partners, shape our strategy, guide our decisions, and help turn science into meaningful progress. We keep it simple, act with urgency, and get it done — expanding access to approved therapies, advancing high-value pipeline programs, and building a leading global rare disease company.

Our vision is simple: a world where people living with rare diseases don’t wait for progress or care. Together with the communities who inspire us, we’re opening new possibilities — proving that breakthroughs aren’t just discovered. They’re created together.

Ready to make a difference? Join us.

What it’s like to work here

At Pharming, every role helps move rare disease therapies closer to the people who need them. We make it happen together, across teams, disciplines, and borders, because breakthroughs don’t happen in silos. Rare diseases are complex, and meaningful progress takes people who ask better questions, challenge each other, and turn insight into action. Here, you won’t work on the sidelines. Pharming is a place for builders, problem-solvers, and bold thinkers who move with urgency, take ownership, and stay focused on what matters most: improving the lives of people living with rare diseases. Advancing rare disease care isn’t the work of one team or one leader. It’s all of us, building what’s next together.